Genetic Disorders Could Be Treated With New CRISPR Technology

The treatment of debilitating inherited disorders is one of the greatest challenges contemporary medicine faces, according to a new study. Despite the renewed optimism that CRISPR technology and improvements in genetic studies have given patients as well as their relatives…
CRISPR Therapy and Genetic Disorders

Recent studies and clinical trials show that NTLA-2001 successfully reduced TTR proteins, considered responsible for ATTR (transthyretin amyloidosis). The NTLA-2001 was used in a clinical study, and this gene-editing technology proved to be a success. Intellia Therapeutics and Regeneron Pharmaceuticals’ conducted…